Growth and Development

Sarafoglou K, Kim MS, Lodish M, Felner EI, Martinerie L, Nokoff NJ, Clemente M, Fechner PY, Vogiatzi MG, Speiser PW, Auchus RJ, Rosales GBG, Roberts E, Jeha GS, Farber RH, Chan JL
Phase 3 Trial of Crinecerfont in Pediatric Congenital Adrenal Hyperplasia.
N Engl J Med. 2024 Aug 8;391(6):493-503
DOI: 10.1056/NEJMoa2404655
IF: 96.3

Bacharier LB, Maspero JF, Katelaris CH, Fiocchi AG, Gagnon R, de Mir I, Guilbert TW, Jackson DJ, Staudinger HW, Laws E, Mannent LP, Akinlade B, Maloney J, Tawo K, Khokhar FA, Li N, Hardin M, Abdulai RM, Lederer DJ, Robinson LB, Bacharier LB, Maspero JF, Katelaris CH, Fiocchi AG, Gagnon R, De Mir I, Guilbert TW, Jackson DJ, Staudinger HW, Laws E, Mannent LP, Akinlade B, Maloney J, Tawo K, Khokhar FA, Li N, Hardin M, Abdulai RM, Lederer DJ, Robinson LB
Assessment of long-term safety and efficacy of dupilumab in children with asthma (LIBERTY ASTHMA EXCURSION): an open-label extension study.
Lancet Respir Med. 2024 Jan;12(1):45-54.
DOI: 10.1016/S2213-2600(23)00303-X.
IF: 38.7

Raidt J, Riepenhausen S, Pennekamp P, Olbrich H, Amirav I, Athanazio RA, Aviram M, Balinotti JE, Bar-On O, Bode SF, Boon M, Borrelli M, Carr SB, Crowley S, Dehlink E, Diepenhorst S, Durdik P, Dworniczak B, Emiralioglu N, Erdem E, Fonnesu R, Gracci S, Grosse-Onnebrink J, Gwozdziewicz K, Haarman EG, Hansen CR, Hogg C, Holgersen MG, Kerem E, Korner RW, Kotz K, Kouis P, Loebinger MR, Lorent N, Lucas JS, Maj D, Mall MA, Marthin JK, Martinu V, Mazurek H, Mitchison HM, Nothe-Menchen T, Ozcelik U, Pifferi M, Pogorzelski A, Ringshausen FC, Roehmel JF, Rovira-Amigo S, Rumman N, Schlegtendal A, Shoemark A, Sperstad Kennelly S, Staar BO, Sutharsan S, Thomas S, Ullmann N, Varghese J, von Hardenberg S, Walker WT, Wetzke M, Witt M, Yiallouros P, Zschocke A, Zietkiewicz E, Nielsen KG, Omran H
Analyses of 1,236 genotyped primary ciliary dyskinesia individuals identify regional clusters of distinct DNA variants and significant genotype-phenotype correlations.
Eur Respir J. 2024 Aug 8;64(2):2301769
DOI: 10.1183/13993003.01769-2023.
IF: 17

Pohunek P, Manali E, Vijverberg S, Carlens J, Chua F, Epaud R, Gilbert C, Griese M, Karadag B, Kerem E, Koucky V, Nathan N, Papiris S, Terheggen-Lagro S, Plch L, Vernetta AT, Bush A
ERS statement on transition of care in childhood interstitial lung diseases.
Eur Respir J. 2024 Aug 15;64(2):2302160
DOI: 10.1183/13993003.02160-2023.
IF: 17

Gramegna A, Addy C, Allen L, Bakkeheim E, Brown C, Daniels T, Davies G, Davies JC, De Marie K, Downey D, Felton I, Hafkemeyer S, Hamouda S, Kendall V, Lindberg U, Macek M, Mayell S, Pearlsman O, Schechter MS, Salvatori L, Sands D, Schwarz C, Shteinberg M, Taylor J, Taylor-Cousar JL, Taylor-Robinson D, Watkins B, Verkleij M, Bevan A, Castellani C, Drevinek P, Gartner S, Lammertyn E, Landau EEC, Middleton PG, Plant BJ, Smyth AR, van Koningsbruggen-R, Burgel PR, Southern KW
Standards for the care of people with cystic fibrosis (CF); Planning for a longer life.
J Cyst Fibros. 2024 May 23:S1569-1993(24)00070-5.
DOI: 10.1016/j.jcf.2024.05.007.
IF: 5.4